Hematopoietic stem cell transplantation may be used to treat a number of conditions both congenital and acquired.
Acquired Malignancies Hematological Leukemias Acute lymphoblastic leukemia (ALL) Acute myeloid leukemia (AML) Chronic lymphocytic leukemia (CLL) Chronic myelogenous leukemia (CML), accelerated phase or blast crisis Lymphomas Hodgkin's disease Non-Hodgkin's lymphoma Myelomas Multiple myeloma (Kahler's disease) Solid tumor cancers Neuroblastoma Desmoplastic small round cell tumor Ewing's sarcoma Choriocarcinoma Hematologic disease Phagocyte disorders Myelodysplasia Anemias Paroxysmal nocturnal hemoglobinuria (PNH; severe aplasia) Aplastic anemia Acquired pure red cell aplasia Myeloproliferative disorders Polycythemia vera Essential thrombocytosis Myelofibrosis Metabolic disorders Amyloidoses Amyloid light chain (AL) amyloidosis Environmentally-induced diseases Radiation poisoning Viral diseases HTLV HIV Autoimmune diseases Multiple sclerosis
Congenital Lysosomal storage disorders Lipidoses (disorders of lipid storage) Neuronal ceroid lipofuscinoses Infantile neuronal ceroid lipofuscinosis (INCL, Santavuori disease,) Jansky–Bielschowsky disease (late infantile neuronal ceroid lipofuscinosis) Sphingolipidoses Niemann–Pick disease Gaucher disease Leukodystrophies Adrenoleukodystrophy Metachromatic leukodystrophy Krabbe disease (globoid cell leukodystrophy) Mucopolysaccharidoses Hurler syndrome (MPS I H, α-L-iduronidase deficiency) Scheie syndrome (MPS I S) Hurler–Scheie syndrome (MPS I H-S) Hunter syndrome (MPS II, iduronidase sulfate deficiency) Sanfilippo syndrome (MPS III) Morquio syndrome (MPS IV) Maroteaux–Lamy syndrome (MPS VI) Sly syndrome (MPS VII) Glycoproteinoses Mucolipidosis II (I-cell disease) Fucosidosis Aspartylglucosaminuria Alpha-mannosidosis Other Wolman disease (acid lipase deficiency) Immunodeficiencies T-cell deficiencies Ataxia-telangiectasia DiGeorge syndrome Combined T- and B-cell deficiencies Severe combined immunodeficiency (SCID), all types Well-defined syndromes Wiskott–Aldrich syndrome Phagocyte disorders Kostmann syndrome Shwachman–Diamond syndrome Immune dysregulation diseases Griscelli syndrome, type II Innate immune deficiencies NF-Kappa-B Essential Modulator (NEMO) deficiency (Inhibitor of Kappa Light Polypeptide Gene Enhancer in B Cells Gamma Kinase deficiency) Hematologic diseases Hemoglobinopathies Sickle cell disease β thalassemia major (Cooley's anemia) Anemias Aplastic anemia Diamond–Blackfan anemia Fanconi anemia Cytopenias Amegakaryocytic thrombocytopenia Hemophagocytic syndromes Hemophagocytic lymphohistiocytosis (HLH)
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