This article contains a list of commercially available gene therapies.
Gene therapies
Alipogene tiparvovec (Glybera): AAV-based treatment for lipoprotein lipase deficiency (no longer commercially available) Axicabtagene ciloleucel (Yescarta): treatment for large B-cell lymphoma Beremagene geperpavec (Vyjuvek): treatment of wounds. Betibeglogene autotemcel (Zynteglo): treatment for beta thalassemia Brexucabtagene autoleucel (Tecartus): treatment for mantle cell lymphoma and acute lymphoblastic leukemia Cambiogenplasmid (Neovasculgen): treatment for vascular endothelial growth factor peripheral artery disease Ciltacabtagene autoleucel (Carvykti): treatment for multiple myeloma Delandistrogene moxeparvovec (Elevidys): treatment for Duchenne muscular dystrophy Elivaldogene autotemcel (Skysona): treatment for cerebral adrenoleukodystrophy Etranacogene dezaparvovec (Hemgenix): AAV-based treatment for hemophilia B Exagamglogene autotemcel (Casgevy): treatment for sickle cell disease. Gendicine: treatment for head and neck squamous cell carcinoma Idecabtagene vicleucel (Abecma): treatment for multiple myeloma Lovotibeglogene autotemcel (Lyfgenia): treatment for sickle cell disease. Marnetegragene autotemcel (Kresladi): treatment of severe leukocyte adhesion deficiency type I. Nadofaragene firadenovec (Adstiladrin): treatment for bladder cancer Obecabtagene autoleucel (Aucatzyl): treatment of acute lymphoblastic leukemia Onasemnogene abeparvovec (Zolgensma): AAV-based treatment for spinal muscular atrophy Pariglasgene brecaparvovec (Genglycos): glycogen storage disease type Ia Prademagene zamikeracel (Zevaskyn): recessive dystrophic epidermolysis bullosa Revakinagene taroretcel (Encelto): treatment of macular telangiectasia type 2 Strimvelis: treatment for adenosine deaminase deficiency (ADA-SCID) Talimogene laherparepvec (Imlygic): treatment for melanoma in people who have recurring skin lesions Tisagenlecleucel (Kymriah): treatment for B cell lymphoblastic leukemia Valoctocogene roxaparvovec (Roctavian): treatment for hemophilia A Voretigene neparvovec (Luxturna): AAV-based treatment for Leber congenital amaurosis
See also FDA-approved CAR T cell therapies
References
External links Daley, Jim (1 January 2020). "Gene Therapy Arrives". Scientific American. Retrieved 9 June 2020.